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Current opinion in pediatrics, 2016-12, Vol.28 (6), p.682-693
2016
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Human gene therapy, 2017-04, Vol.28 (4), p.314
2017
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Journal of inherited metabolic disease, 2012-01, Vol.35 (1), p.91-102
2012
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Journal of inherited metabolic disease, 2012-01, Vol.35 (1), p.103-114
2012
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Cell reports (Cambridge), 2017-12, Vol.21 (12), p.3548-3558
- An, Ding
- Schneller, Jessica L.
- Frassetto, Andrea
- Liang, Shi
- Zhu, Xuling
- Park, Ji-Sun
- Theisen, Matt
- Hong, Sue-Jean
- Zhou, Jenny
- Rajendran, Raj
- Levy, Becca
- Howell, Rebecca
- Besin, Gilles
- Presnyak, Vladimir
- Sabnis, Staci
- Murphy-Benenato, Kerry E.
- Kumarasinghe, E. Sathyajith
- Salerno, Timothy
- Mihai, Cosmin
- Lukacs, Christine M.
- Chandler, Randy J.
- Guey, Lin T.
- Venditti, Charles P.
- Martini, Paolo G.V.
2017
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Nature biotechnology, 2021-01, Vol.39 (1), p.24-26
2021
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The Journal of pediatrics, 2015-06, Vol.166 (6), p.1346-1350
2015
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Nature genetics, 2015-04, Vol.47 (4), p.338-344
- Izumi, Kosuke
- Nakato, Ryuichiro
- Zhang, Zhe
- Edmondson, Andrew C
- Noon, Sarah
- Dulik, Matthew C
- Rajagopalan, Ramakrishnan
- Venditti, Charles P
- Gripp, Karen
- Samanich, Joy
- Zackai, Elaine H
- Deardorff, Matthew A
- Clark, Dinah
- Allen, Julian L
- Dorsett, Dale
- Misulovin, Ziva
- Komata, Makiko
- Bando, Masashige
- Kaur, Maninder
- Katou, Yuki
- Shirahige, Katsuhiko
- Krantz, Ian D
2015
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American journal of human genetics, 2013-09, Vol.93 (3), p.506-514
- Yu, Hung-Chun
- Sloan, Jennifer L.
- Scharer, Gunter
- Brebner, Alison
- Quintana, Anita M.
- Achilly, Nathan P.
- Manoli, Irini
- Coughlin, Curtis R.
- Geiger, Elizabeth A.
- Schneck, Una
- Watkins, David
- Suormala, Terttu
- Van Hove, Johan L.K.
- Fowler, Brian
- Baumgartner, Matthias R.
- Rosenblatt, David S.
- Venditti, Charles P.
- Shaikh, Tamim H.
2013
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Molecular metabolism (Germany), 2016-10, Vol.5 (10), p.926-936
2016
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Ophthalmology (Rochester, Minn.), 2016-03, Vol.123 (3), p.571-582
2016
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Proceedings of the National Academy of Sciences - PNAS, 2013-08, Vol.110 (33), p.13552-13557
- Manoli, Irini
- Sysol, Justin R.
- Li, Lingli
- Houillier, Pascal
- Garone, Caterina
- Wang, Cindy
- Zerfas, Patricia M.
- Cusmano-Ozog, Kristina
- Young, Sarah
- Trivedi, Niraj S.
- Cheng, Jun
- Sloan, Jennifer L.
- Chandler, Randy J.
- Abu-Asab, Mones
- Tsokos, Maria
- Elkahloun, Abdel G.
- Rosen, Seymour
- Enns, Gregory M.
- Berry, Gerard T.
- Hoffmann, Victoria
- DiMauro, Salvatore
- Schnermann, Jurgen
- Venditti, Charles P.
2013
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Molecular therapy, 2010-01, Vol.18 (1), p.11-16
2010
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Science advances, 2019-08, Vol.5 (8), p.eaaw8357-eaaw8357
2019
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The American journal of clinical nutrition, 2011, Vol.93 (1), p.47-56
2011
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Molecular therapy. Methods & clinical development, 2021-03, Vol.20, p.247-257
2021
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Journal of inherited metabolic disease, 2024-01, Vol.47 (1), p.5-6
2024
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Pediatrics (Evanston), 2012-06, Vol.129 (6), p.e1541
2012
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Molecular therapy. Methods & clinical development, 2023-09, Vol.30, p.181-190
2023
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Molecular therapy. Methods & clinical development, 2022-12, Vol.27, p.61-72
2022
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Human gene therapy, 2019-10, Vol.30 (10), p.1236
2019
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Molecular therapy. Methods & clinical development, 2021-09, Vol.22, p.279-292
2021
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Molecular therapy. Methods & clinical development, 2021-12, Vol.23, p.619-632
2021
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Journal of inherited metabolic disease, 2024-01, Vol.47 (1), p.63-79
2024
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Molecular therapy. Methods & clinical development, 2021-06, Vol.21, p.765-776
2021
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- Journal Of Inherited Metabolic Disease
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