Sortiert nach
Molecular therapy, 2014-02, Vol.22 (2), p.338-347
2014
Volltextzugriff (PDF)
The New England journal of medicine, 2017-11, Vol.377 (18), p.1713-1722
- Mendell, Jerry R.
- Al-Zaidy, Samiah
- Shell, Richard
- Arnold, W. Dave
- Rodino-Klapac, Louise R.
- Prior, Thomas W.
- Lowes, Linda
- Alfano, Lindsay
- Berry, Katherine
- Church, Kathleen
- Kissel, John T.
- Nagendran, Sukumar
- L’Italien, James
- Sproule, Douglas M.
- Wells, Courtney
- Cardenas, Jessica A.
- Heitzer, Marjet D.
- Kaspar, Allan
- Corcoran, Sarah
- Braun, Lyndsey
- Likhite, Shibi
- Miranda, Carlos
- Meyer, Kathrin
- Foust, K.D.
- Burghes, Arthur H.M.
- Kaspar, Brian K.
2017
Volltextzugriff (PDF)
Lack of toxicity of alpha-sarcoglycan overexpression supports clinical gene transfer trial in LGMD2D
2008
Volltextzugriff (PDF)
Gene therapy, 2016-01, Vol.23 (1), p.57-66
2016
Volltextzugriff (PDF)
Canadian journal of neurological sciences, 2024-06, Vol.51 (s1), p.S9-S10
2024
Volltextzugriff (PDF)
The New England journal of medicine, 2017-11, Vol.377 (18), p.1713-1722
- Mendell, Jerry R
- Al-Zaidy, Samiah
- Shell, Richard
- Arnold, W. Dave
- Rodino-Klapac, Louise R
- Prior, Thomas W
- Lowes, Linda
- Alfano, Lindsay
- Berry, Katherine
- Church, Kathleen
- Kissel, John T
- Nagendran, Sukumar
- L’Italien, James
- Sproule, Douglas M
- Wells, Courtney
- Cardenas, Jessica A
- Heitzer, Marjet D
- Kaspar, Allan
- Corcoran, Sarah
- Braun, Lyndsey
- Likhite, Shibi
- Miranda, Carlos
- Meyer, Kathrin
- Foust, K.D
- Burghes, Arthur H.M
- Kaspar, Brian K
2017
Volltextzugriff (PDF)
Molecular therapy, 2014-03, Vol.22 (3), p.511-521
2014
Volltextzugriff (PDF)
Gene therapy, 2016-01, Vol.23 (1), p.57
2016
Volltextzugriff (PDF)
Developmental biology, 2004-09, Vol.273 (2), p.308-320
2004
Volltextzugriff (PDF)
Annals of neurology, 2013-11, Vol.74 (5), p.637-647
- Mendell, Jerry R.
- Rodino-Klapac, Louise R.
- Sahenk, Zarife
- Roush, Kandice
- Bird, Loren
- Lowes, Linda P.
- Alfano, Lindsay
- Gomez, Ann Maria
- Lewis, Sarah
- Kota, Janaiah
- Malik, Vinod
- Shontz, Kim
- Walker, Christopher M.
- Flanigan, Kevin M.
- Corridore, Marco
- Kean, John R.
- Allen, Hugh D.
- Shilling, Chris
- Melia, Kathleen R.
- Sazani, Peter
- Saoud, Jay B.
- Kaye, Edward M.
2013
Volltextzugriff (PDF)
Molecular therapy, 2021-02, Vol.29 (2), p.464-488
2021
Volltextzugriff (PDF)
Annals of neurology, 2023-11, Vol.94 (5), p.955-968
2023
Volltextzugriff (PDF)
Human gene therapy, 2021-04, Vol.32 (7-8), p.375
2021
Volltextzugriff (PDF)
Annals of neurology, 2016-02, Vol.79 (2), p.257-271
2016
Volltextzugriff (PDF)
Human gene therapy, 2021-04, Vol.32 (7-8), p.390
2021
Volltextzugriff (PDF)
PloS one, 2012-06, Vol.7 (6), p.e39233-e39233
2012
Volltextzugriff (PDF)
Human molecular genetics, 2013-12, Vol.22 (24), p.4929-4937
2013
Volltextzugriff (PDF)
Human gene therapy, 2018-07, Vol.29 (7), p.749
2018
Volltextzugriff (PDF)
Molecular therapy, 2014-04, Vol.22 (4), p.713-724
- Chicoine, Louis G.
- Rodino-Klapac, Louise R.
- Shao, Guohong
- Xu, Rui
- Bremer, William G.
- Camboni, Marybeth
- Golden, Bethannie
- Montgomery, Chrystal L.
- Shontz, Kimberly
- Heller, Kristin N.
- Griffin, Danielle A.
- Lewis, Sarah
- Coley, Brian D.
- Walker, Christopher M.
- Clark, K. Reed
- Sahenk, Zarife
- Mendell, Jerry R.
- Martin, Paul T.
2014
Volltextzugriff (PDF)
Molecular therapy. Methods & clinical development, 2024-03, Vol.32 (1), p.101195-101195, Article 101195
2024
Volltextzugriff (PDF)
Science translational medicine, 2009-11, Vol.1 (6), p.6ra15
2009
Volltextzugriff (PDF)
Human gene therapy, 2017-06, Vol.28 (6), p.493
2017
Volltextzugriff (PDF)
Annals of clinical and translational neurology, 2015-03, Vol.2 (3), p.256-270
2015
Volltextzugriff (PDF)
Journal of translational medicine, 2007-09, Vol.5 (1), p.45-45, Article 45
2007
Volltextzugriff (PDF)
Frontiers in cell and developmental biology, 2023-07, Vol.11, p.1167762-1167762
- Mendell, Jerry R
- Shieh, Perry B
- McDonald, Craig M
- Sahenk, Zarife
- Lehman, Kelly J
- Lowes, Linda P
- Reash, Natalie F
- Iammarino, Megan A
- Alfano, Lindsay N
- Sabo, Brenna
- Woods, Jeremy D
- Skura, Christy L
- Mao, Howard C
- Staudt, Loretta A
- Griffin, Danielle A
- Lewis, Sarah
- Wang, Shufang
- Potter, Rachael A
- Singh, Teji
- Rodino-Klapac, Louise R
2023
Volltextzugriff (PDF)
Suchergebnisse filtern
Filter anzeigenNur zeigen
Publikationsform
Erscheinungsjahr
n.n
n.n
Thema
- Science & Technology
- Life Sciences & Biomedicine
- Gene Therapy
- Animals
- Muscular Dystrophy
- Humans
- Medicine, Research & Experimental
- Research & Experimental Medicine
- Dependovirus - Genetics
- Mice
- Genetics & Heredity
- Mutation
- Biotechnology & Applied Microbiology
- Disease Models, Animal
- Dystrophin - Genetics
- Adeno-Associated Virus
- Genetic Therapy - Methods
- Gene Expression
- Gene Transfer Techniques
- Genetic Therapy
Kollektion
- Ingenta
- Elsevier ScienceDirect Journals Complete
- EZB Free E-Journals
- Elsevier Journal Backfiles on ScienceDirect (DFG Nationallizenzen)
- MEDLINE
- Journals@Ovid Complete
- NUS Single-Journal Subscriptions
- IngentaConnect Journals
- Wiley Online Library Journals Frontfile Complete
- Wiley Online Library Full Collection 2018
- Springer Nature - Connect here FIRST to enable access
- Springer Book Series
- PAIS Index
- Cambridge Journals Online (DEFF)
- Business Source Ultimate
- Oxford Journals
- Science Online科学在线
- Oxford Journals 2020 Medicine
- SpringerLink_现刊
- Taylor & Francis Journals Auto-Holdings Collection
Zeitschrift / Serie
- Neuromuscular Disorders : Nmd
- Molecular Therapy
- Human Gene Therapy
- Molecular Therapy. Methods & Clinical Development
- Annals Of Neurology
- The American Journal Of Pathology
- The New England Journal Of Medicine
- American Journal Of Physiology: Cell Physiology
- American Journal Of Respiratory And Critical Care Medicine
- Gene Therapy