UB Paderborn / Katalog / Suche / in CDI

1 – 25 von 144

Sortiert nach

Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott-Aldrich syndrome

Nature Medicine, 2022-01, Vol.28 (1), p.71-80

2022

Link zum Volltext

Verfügbarkeit prüfen

Progress and prospects: gene therapy for inherited immunodeficiencies

Gene therapy, 2009-11, Vol.16 (11), p.1285-1291

2009

Link zum Volltext

Verfügbarkeit prüfen

Validation of a mutated PRE sequence allowing high and sustained transgene expression while abrogating WHV-X protein synthesis: application to the gene therapy of WAS

Gene therapy, 2009-05, Vol.16 (5), p.605-619

2009

Link zum Volltext

Verfügbarkeit prüfen

Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients

Gene therapy, 2007-03, Vol.14 (5), p.415-428

2007

Link zum Volltext

Verfügbarkeit prüfen

Scale-up and manufacturing of clinical-grade self-inactivating γ-retroviral vectors by transient transfection

Gene therapy, 2012-03, Vol.19 (3), p.246-254

2012

Link zum Volltext

Verfügbarkeit prüfen

Inhibition of retinal neovascularisation by gene transfer of soluble VEGF receptor sFlt-1

Gene therapy, 2002-03, Vol.9 (5), p.320-326

2002

Link zum Volltext

Verfügbarkeit prüfen

Efficient gene delivery to the adult and fetal CNS using pseudotyped non-integrating lentiviral vectors

Gene therapy, 2009-04, Vol.16 (4), p.509-520

2009

Link zum Volltext

Verfügbarkeit prüfen

Long-term preservation of retinal function in the RCS rat model of retinitis pigmentosa following lentivirus-mediated gene therapy

Gene therapy, 2005-04, Vol.12 (8), p.694-701

2005

Link zum Volltext

Verfügbarkeit prüfen

Critical Variables affecting clinical-grade production of the self-inactivating gamma-retroviral vector for the treatment of X-linked severe combined immunodeficiency

Gene therapy, 2012-08, Vol.19 (8), p.872-876

2012

Link zum Volltext

Verfügbarkeit prüfen

Lentiviral transduction of the murine lung provides efficient pseudotype and developmental stage-dependent cell-specific transgene expression

Gene therapy, 2008-08, Vol.15 (16), p.1167-1175

2008

Link zum Volltext

Verfügbarkeit prüfen

In vivo gene transfer to the mouse eye using an HIV-based lentiviral vector; efficient long-term transduction of corneal endothelium and retinal pigment epithelium

Gene therapy, 2001-11, Vol.8 (21), p.1665-1668

2001

Link zum Volltext

Verfügbarkeit prüfen

Lentiviral vectors transcriptionally targeted to hematopoietic cells by WASP gene proximal promoter sequences

Gene therapy, 2005-04, Vol.12 (8), p.715-723

2005

Link zum Volltext

Verfügbarkeit prüfen

Correction of SCID-X1 using an enhancerless Vav promoter

Human gene therapy, 2011-03, Vol.22 (3), p.263

2011

Link zum Volltext

Verfügbarkeit prüfen

Permanent partial phenotypic correction and tolerance in a mouse model of hemophilia B by stem cell gene delivery of human factor IX

Gene therapy, 2006-01, Vol.13 (2), p.117-126

2006

Link zum Volltext

Verfügbarkeit prüfen

Current progress on gene therapy for primary immunodeficiencies

Gene therapy, 2013-10, Vol.20 (10), p.963-969

2013

Link zum Volltext

Verfügbarkeit prüfen

Cell-specific and efficient expression in mouse and human B cells by a novel hybrid immunoglobulin promoter in a lentiviral vector

Gene therapy, 2007-12, Vol.14 (23), p.1623-1631

2007

Link zum Volltext

Verfügbarkeit prüfen

Stable rAAV-mediated transduction of rod and cone photoreceptors in the canine retina

Gene therapy, 2003-08, Vol.10 (16), p.1336-1344

2003

Link zum Volltext

Verfügbarkeit prüfen

Hypoxia-regulated transgene expression in experimental retinal and choroidal neovascularization

Gene therapy, 2003-06, Vol.10 (12), p.1049-1054

2003

Link zum Volltext

Verfügbarkeit prüfen

Gene therapy progress and prospects: gene therapy for severe combined immunodeficiency

Gene therapy, 2003-11, Vol.10 (24), p.1999-2004

2003

Link zum Volltext

Verfügbarkeit prüfen

Progress and Prospects: Gene Therapy Clinical Trials (Part 1)

Gene therapy, 2007-10, Vol.14 (20), p.1439-1447

2007

Link zum Volltext

Verfügbarkeit prüfen

T cell transduction and suicide with an enhanced mutant thymidine kinase

Gene therapy, 2002-06, Vol.9 (12), p.824-827

2002

Link zum Volltext

Verfügbarkeit prüfen

Intraocular gene delivery of ciliary neurotrophic factor results in significant loss of retinal function in normal mice and in the Prph2 model of retinal degeneration

Gene therapy, 2003-03, Vol.10 (6), p.523-527

2003

Link zum Volltext

Verfügbarkeit prüfen

Efficient and Selective AAV2-Mediated Gene Transfer Directed to Human Vascular Endothelial Cells

Molecular therapy, 2001-09, Vol.4 (3), p.174-181

2001

Link zum Volltext

Verfügbarkeit prüfen

High-titer recombinant adeno-associated virus production from replicating amplicons and herpes vectors deleted for glycoprotein H

Human gene therapy, 1999-10, Vol.10 (15), p.2527-2537

1999

Link zum Volltext

Verfügbarkeit prüfen

1 – 25 von 144

Suche als RSS-Feed

Aktive Filter

ThemaResearch & Experimental Medicine

Suchergebnisse filtern

Filter anzeigen

Nur zeigen

Geprüft (Peer-Review)
(143)
Mit Volltextzugriff
(116)

Publikationsform

Artikel
(144)

Sprache

Englisch
(144)
Japanisch
(34)

Erscheinungsjahr

n.n

Thema

Life Sciences & Biomedicine
(144)
Medicine, Research & Experimental
(144)
Science & Technology
(144)
Biotechnology & Applied Microbiology
(103)
Gene Therapy
(99)
Genetics & Heredity
(97)
Humans
(95)
Animals
(74)
Mice
(56)
Genetic Therapy - Methods
(49)
Gene Expression
(42)
Lentivirus - Genetics
(40)
Genetic Vectors - Genetics
(37)
Vectors
(35)
Biochemistry & Molecular Biology
(34)
Immunology
(33)
Biological And Medical Sciences
(32)
Biotechnology
(32)
Fundamental And Applied Biological Sciences. Psychology
(31)

14 weitere anzeigen...

Weniger anzeigen...

Menü

Weitere Dienste

Einstellungen

Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott-Aldrich syndrome

Progress and prospects: gene therapy for inherited immunodeficiencies

Validation of a mutated PRE sequence allowing high and sustained transgene expression while abrogating WHV-X protein synthesis: application to the gene therapy of WAS

Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients

Scale-up and manufacturing of clinical-grade self-inactivating γ-retroviral vectors by transient transfection

Inhibition of retinal neovascularisation by gene transfer of soluble VEGF receptor sFlt-1

Efficient gene delivery to the adult and fetal CNS using pseudotyped non-integrating lentiviral vectors

Long-term preservation of retinal function in the RCS rat model of retinitis pigmentosa following lentivirus-mediated gene therapy

Critical Variables affecting clinical-grade production of the self-inactivating gamma-retroviral vector for the treatment of X-linked severe combined immunodeficiency

Lentiviral transduction of the murine lung provides efficient pseudotype and developmental stage-dependent cell-specific transgene expression

In vivo gene transfer to the mouse eye using an HIV-based lentiviral vector; efficient long-term transduction of corneal endothelium and retinal pigment epithelium

Lentiviral vectors transcriptionally targeted to hematopoietic cells by WASP gene proximal promoter sequences

Correction of SCID-X1 using an enhancerless Vav promoter

Permanent partial phenotypic correction and tolerance in a mouse model of hemophilia B by stem cell gene delivery of human factor IX

Current progress on gene therapy for primary immunodeficiencies

Cell-specific and efficient expression in mouse and human B cells by a novel hybrid immunoglobulin promoter in a lentiviral vector

Stable rAAV-mediated transduction of rod and cone photoreceptors in the canine retina

Hypoxia-regulated transgene expression in experimental retinal and choroidal neovascularization

Gene therapy progress and prospects: gene therapy for severe combined immunodeficiency

Progress and Prospects: Gene Therapy Clinical Trials (Part 1)

T cell transduction and suicide with an enhanced mutant thymidine kinase

Intraocular gene delivery of ciliary neurotrophic factor results in significant loss of retinal function in normal mice and in the Prph2 model of retinal degeneration

Efficient and Selective AAV2-Mediated Gene Transfer Directed to Human Vascular Endothelial Cells

High-titer recombinant adeno-associated virus production from replicating amplicons and herpes vectors deleted for glycoprotein H

Lentiviral gene therapy for X-linked chronic granulomatous disease

Aktive Filter

Suchergebnisse filtern